Regenxbio is pitching at FDA approval next year for its Duchenne muscular dystrophy (DMD) gene therapy RGX-202, after ...

Regenxbio’s gene therapy for Duchenne muscular dystrophy has smashed the primary endpoint of its pivotal trial, securing a win for a biotech that has struggled in recent months under the weight of a ...

Gene editing can repair a DNA error in mice that causes Dravet syndrome, a rare, incurable, and potentially deadly form of ...

A recent study shows altered gene expression associated with brain arteriovenous malformation pathogenesis in HMEC‑1 ...

Scientists have uncovered evidence supporting a mechanism in which transposable elements (TEs), once considered ...

Opus Genetics Virtual R&D Science Forum Scheduled for Tuesday, June 16, 2026, at 10:00 am ETUpcoming Data Readout for Cohort 1 of OPGx-BEST1 ...

A federal judge canceled next week’s jury trial over claims Curio Bioscience Inc.’s tissue-mapping kits infringe five spatial ...

Spengler, Ph.D., explains gene regulatory networks: the complex biological systems that control which genes turn on, which genes turn off, and how cells develop specialized identities during embryonic ...

Scientists at the University of Rochester pulled off a remarkable experiment: they transferred a longevity-related gene from ...

Happy birthday, David Attenborough! Born May 8, 1926, nature’s greatest hype man has now lived a full century and counting. No small feat, especially since ONS data shows that men make up only 20% of ...

The ARVO poster presentation and a video recording of Dr. Pennesi’s summary of Cohort 1 Baseline Demographics and Key ...

To be presented at the 2026 ASGCT conference in Boston, MA TAMPA, FL, UNITED STATES, April 30, 2026 /EINPresswire.com/ ...